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  • FDA Approves First Treatment for Molybdenum Cofactor Deficiency Type A americanpharmaceuticalreview
    March 05, 2021
    The U.S. Food and Drug Administration (FDA) approved Nulibry (fosdenopterin) for injection to reduce the risk of death due to Molybdenum Cofactor Deficiency Type A, a rare, genetic, metabolic disorder that typically presents in the first few days of ...
  • FDA approves Nulibry to treat Molybdenum Cofactor Deficiency Type A pharmatimes
    March 02, 2021
    The US Food and Drug Administration (FDA) has approved BridgeBio Pharma and Origin Biosciences’ Nulibry (fosdenopterin), making it the first treatment to be authorised to reduce the risk of mortality in patients with molybdenum cofactor deficiency ...
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